Stem cell therapy fast tracked beta thalassemia

The FDA has given a fast track designation for CTX001 for its Treatment of transfusion-dependent beta-thalassemia. TDT is a serious, innovative type of Betathalassemia characterized By acute anemia, transfusion addiction, inevitable iron overload, acute comorbidities, and also a shorter life span as well as the overall populace. Patients who have TDT desire life-long supportive attention and has to undergo blood transfusions every couple of weeks to alleviate nausea and empower survival. Currently, allogeneic hematopoietic stem cell transplant would be your only real remedy option together with all the potential to Fix the hereditary Lack in TDT.

Our most popular topics on